Search for Clinical Trial Results
Ceroid Storage Disease - 21 Studies Found
Status | Study |
Recruiting |
Study Name: Clinical and Neuropsychological Investigations in Batten Disease Condition: Neuronal Ceroid Lipofuscinosis Date: 2013-05-17 |
Terminated |
Study Name: Collection of Cerebrospinal Fluid in Healthy Children Condition:
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Recruiting |
Study Name: Batten CLN6 Gene Therapy Condition:
Date: 2016-03-16 Interventions: Drug: scAVV9.CB.CLN6 Six subjects with diagnosis of CLN6 disease will receive scAVV9.CB.CLN6 administere |
Completed |
Study Name: Genotype - Phenotype Correlations of LINCL Condition:
Date: 2005-09-06 |
Active, not recruiting |
Study Name: A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease Condition:
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Enrolling by invitation |
Study Name: A Safety, Tolerability, and Efficacy Study of Intracerebroventricular BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease Condition:
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Recruiting |
Study Name: Genetic Characterization of Movement Disorders and Dementias Condition:
Date: 2015-04-03 |
Recruiting |
Study Name: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condition:
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Recruiting |
Study Name: Human Placental-Derived Stem Cell Transplantation Condition:
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